WASHINGTON - The pharmaceutical industry won approval to market a record number of new drugs for rare diseases last year, as a combination of scientific innovation and business opportunity spurred new treatments for diseases long-ignored by drug companiesDrug companies are increasingly taking adva More …

A new study uses a mouse model of a human autoimmune disease to reveal how abnormal regulation of the intracellular sensors that detect invading viruses can lead to autoimmune pathologyThe research, published online on January 26th in the journal Immunity by Cell Press, provides key insight into m More …

BioMarin Pharmaceutical Inc.,  with five drugs in clinical trials, is seeking to buy smaller companies to expand its pipeline for treatment of rare diseases, not be acquired itself, Chief Executive Officer Jean-Jacques Bienaime said in an interviewThe number of trials is the most ever at one time More …