10th Annual Congress on Rare Diseases and Orphan Drugs, Toronto (2019)

3.0 from 3 votes
Date: 23 - 24 September, 2019
Location: Toronto, Canada

On behalf of the organizing committee, we are pleased to announce that the 10th Annual Congress on Rare Diseases and Orphan Drugs (Rare Diseases 2019) will be held from September 23-24, 2019 in Toronto, Canada. Rare Diseases 2019 provides a premier interdisciplinary platform for researchers to present the latest research findings and describe emerging technologies, and directions in rare diseases and orphan drugs issues. The conference seeks to contribute to presenting novel research results in all aspects of Rare Diseases and Orphan Drugs.

The conference aims to bring together leading academic scientists, researchers and research scholars to exchange and share their experiences and research results about all aspects of rare diseases and orphan drugs. It also provides the premier interdisciplinary forum for scientists, professors, specialists, researchers, students and practitioners to present their latest research results, ideas, developments, and applications in all areas of rare diseases and orphan drugs. The conference will bring together leading academic scientists, researchers, Industrial delegates Healthcare Professionals and scholars in the domain of interest from around the world.

The conference's goal will to provide a scientific forum for all international prestige scholars around the world and enable the interactive exchange of state-of-the-art knowledge. The conference will focus on evidence-based benefits proven in clinical trials and scientific experiments.

Why to attend?

Join the Rare Diseases and Orphan Drugs Congress to keep up to date with the industry and to learn from our expert speaker panel, bringing you important new case studies and reports on this year's relevant topics.
  • Learn more about global trends in rare diseases and its advances in the therapeutic and diagnostic market.
  • Discussing strategic win-win collaborations to help accelerate rare disease clinical drug development, and improve relationships between drug developers and patients to consider both parties interests
  • Hear more about how patient engagement by integrating the patient perspective into the drug development process through patient advocacy, patient-centric research, and patient groups
  • Learn about how the regulatory landscape for drug approvals is different between countries, and why it is important to keep informed about the regulations and guidelines of each region
  • Gain knowledge of different rare diseases and their unique challenges, as well as how treatment methods can be transferred to other rare diseases
  • Introducing cell and gene therapies to rare disease treatment - learn how gene therapy methods can improve the treatment of rare diseases and why it is becoming more commercially successful


Market Analysis

Importance and Scope
A rare/orphan disease is outlined as a condition that affects fewer than 200,000 people. This definition was created by Congress within the Orphan Drug Act of 1983. There may be as many as 7,000 rare diseases and 70% of them have no form of treatment. Regulatory edges like longer market exclusivity, breakthrough designations, reduced fees and tax incentives are all encouraging investment. However, the marketing process and lifecycle for a rare disease drug are very different to a mass market product and require particular skills and knowledge.

Rare Diseases 2019 will be the best platform for all the doctors, researchers, renowned Scientists, research scholars, students who are working in this field across the globe under a single roof to exchange their knowledge related to Rare Diseases and Orphan Drugs. This international event is an effort to find an alternative for invasive imaging technique against rare diseases like Zellweger syndrome, Muscular Dystrophy, Alkaptonuria, Angelman syndrome, Prader-Willi syndrome, Tay Sachs disease, Fragile X syndrome, Gaucher disease as well as many others.

Conference Highlights 

      • Different types of Rare Diseases
      • Clinical Research and Public Awareness
      • Mystery Diagnosis of Rare Diseases
      • Challenges in Rare Diseases Treatment
      • Rare Infectious Diseases and Immune Deficiencies
      • Rare Diseases in Cancer
      • Rare Diseases in Aging
      • Orphan Drugs- development trends and strategies
      • Clinical Research on Orphan Drugs
      • Orphan Drugs and Ethical Issues
      • Future Hereditary of Rare Diseases and Orphan Drugs
      • Patient organizations and their role in drug development or clinical research


3.0 from 3 votes