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Treatment Database

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Product Indication Date Designated
transforming growth factor beta trap/anti-programmed death ligand-1 antibody bifunctional fusion protein Biliary tract cancer Dec 07, 2018
messenger ribonucleic acid-based therapeutic agent encoding human propionyl-CoA carboxylase alpha and beta subunits Propionic acidemia Dec 05, 2018
99mTc-HYNIC-[D-Phe1,Tyr3-Octreotide] trifluoroacetate Diagnostic for the management of neuroendocrine tumors Dec 05, 2018
(+)-alpha-dihydrotetrabenazine Huntington's disease Dec 05, 2018
self-complementary non-replicating, recombinant adeno-associated virus serotype rhesus 74 expressing the human alpha-sarcoglycan gene under a triple E-box muscle creatine kinase muscle specific promoter (scAAVrh74.tMCK.hSGCA) Limb girdle muscular dystrophy Type 2D Dec 05, 2018
recombinant human interleukin 12 Pancreatic cancer Dec 05, 2018
doranidazole Radiosensitizer to be used during radiation treatment of pancreatic cancer Nov 30, 2018
(1S, 4R, 5R, 7S)-3, 4-dibenzyl-2-oxo-6, 8-dioxa- 3-azabyciclo [3.2.1] octane-7-carboxylic acid-L-lysine Neurotrophic keratopathy Nov 30, 2018
terlipressin Hepatorenal syndrome Nov 21, 2018
benralizumab Eosinophilic granulomatosis with polyangiitis Nov 21, 2018
hydromethylthionine mesylate Frontotemporal dementia Nov 20, 2018
humanized anti-Globo H monoclonal antibody Pancreatic cancer Nov 20, 2018
recombinant adeno-associated virus (AAV) vector based on the AAV serotype hu37 containing a single stranded DNA genome encoding a form of human Factor VIII Hemophilia A Nov 20, 2018
peptide-drug conjugate combining [(Tyr3,Cys8) octreotate amide] and N2'-deacetyl-N2'-(3-mercapto-1-oxopropyl) maytansine Neuroendocrine tumors Nov 20, 2018
8-bromo-2-(1-methylpiperidin-4-yl) amino)-4-(4-phenoxyphenyl) amino) pyrido[4,3-d] pyrimidin-5(6H)-one hydrochloride Acute Myeloid Leukemia Nov 20, 2018
flunarizine Alternating Hemiplegia Nov 20, 2018
small molecule inhibitor of integrins av�6 and av�1 Primary sclerosing cholangitis Nov 19, 2018
humanized IgG1 antibody specifific for the AXL tyrosine kinase conjugated to monomethyl auristatin E Pancreatic cancer Nov 19, 2018
Ex vivo fused normal allogeneic human myoblast with autologous human myoblast derived from Duchenne muscular dystrophy affected donor Duchenne muscular dystrophy Nov 19, 2018
Ex vivo fused normal allogeneic human myoblast with another normal allogeneic human myoblast Duchenne muscular dystrophy Nov 19, 2018