2′-O-methyl phosphorothioate 5′-GCUAGGUUUACGGGACCUCU-3′

2′-O-methyl phosphorothioate 5′-GCUAGGUUUACGGGACCUCU-3′
Trade Name
Orphan Indication Amyotrophic lateral sclerosis
USA Market Approval USA
USA Designation Date 2012-10-31 00:00:00
Sponsor LifeSplice Pharma LLC;1 Great Valley Parkway, Suite 20;Malvern, Pennsylvania, 19355