Modified messenger ribonucleic acid encoding human ornithine transcarbamylase enzyme encapsulated into lipid nanoparticles

Modified messenger ribonucleic acid encoding human ornithine transcarbamylase enzyme encapsulated into lipid nanoparticles
Trade Name
Orphan Indication Ornithine Transcarbamylase Deficiency
EU Market Approval EU
EU Designation Date 2017-04-20 00:00:00
Sponsor PhaseRx Ireland, Ltd