Modified messenger ribonucleic acid encoding human argininosuccinate lyase enzyme encapsulated into lipid nanoparticles

Modified messenger ribonucleic acid encoding human argininosuccinate lyase enzyme encapsulated into lipid nanoparticles
Trade Name
Orphan Indication Argininosuccinic Aciduria
EU Market Approval EU
EU Designation Date 2017-12-12 00:00:00
Sponsor PhaseRx Ireland, Ltd