Recombinant adeno-associated virus retinal pigment epithelium gene vector AAV2-hRPE65v2

Recombinant adeno-associated virus retinal pigment epithelium gene vector AAV2-hRPE65v2
Trade Name
Orphan Indication Leber congenital amaurosis
USA Market Approval USA
USA Designation Date 2008-06-24 00:00:00
Sponsor Spark Therapeutics, Inc.;3737 Market Street, Suite 1300;Philadelphia, Pennsylvania, 19104