Adeno-associated viral vector expressing human acid alpha glucosidase gene

Adeno-associated viral vector expressing human acid alpha glucosidase gene
Trade Name
Orphan Indication Pompe disease
USA Market Approval USA
USA Designation Date 2007-03-20 00:00:00
Sponsor Audentes Therapeutics, Inc.;101 Montgomery St., #2650;San Francisco, California, 94104