recombinant adeno-associated virus serotype 9 vector containing the transgene UBE3A encoding for ubiquitin protein ligase E3A/E6-AP

recombinant adeno-associated virus serotype 9 vector containing the transgene UBE3A encoding for ubiquitin protein ligase E3A/E6-AP
Trade Name
Orphan Indication Angelman syndrome
USA Market Approval USA
USA Designation Date 2015-10-29 00:00:00
Sponsor Agilis Biotherapeutics, LLC;245 First Street, Suite 1800;Cambridge, Massachusetts, 02142