adeno associated virus with modified transthyretin and sequence encoding factor IX variant gene

adeno associated virus with modified transthyretin and sequence encoding factor IX variant gene
Trade Name
Orphan Indication Hemophilia B
USA Market Approval USA
USA Designation Date 2014-03-14 00:00:00
Sponsor Baxalta US, Inc.;One Baxter Way;Westlake Village, California, 91362