Heptadecasodium salt of an 18-base residue phosphorothioate oligonucleotide

Heptadecasodium salt of an 18-base residue phosphorothioate oligonucleotide
Trade Name
Orphan Indication Spinal muscular atrophy
USA Market Approval USA
USA Designation Date 2011-04-18 00:00:00
Sponsor Isis Pharmaceuticals, Inc.;1896 Rutherford Road;Carlsbad, CA, 92008