One, two, three, or four antisense oligonucleotides of Phosphorodiamidate morpholino oligomer combination that skips exons 4, 5, 6, and 7 of the gamma sarcoglycan (SGCG) gene

One, two, three, or four antisense oligonucleotides of Phosphorodiamidate morpholino oligomer combination that skips exons 4, 5, 6, and 7 of the gamma sarcoglycan (SGCG) gene
Trade Name
Orphan Indication Limb-girdle muscular dystrophy
USA Market Approval USA
USA Designation Date 2017-07-18 00:00:00
Sponsor Kurt+Peter Foundation;P. O. Box 691;Menlo Park, California, 94025