adeno-associated virus serotype 9 expressing the human Survival Motor Neuron gene

adeno-associated virus serotype 9 expressing the human Survival Motor Neuron gene
Trade Name
Orphan Indication Spinal muscular atrophy
USA Market Approval USA
USA Designation Date 2014-09-30 00:00:00
Sponsor AveXis, Inc.;One Energy Square, Suite 604;Dallas, Texas, 75206