adeno-associated viral vector containing modified U11 snRNA

adeno-associated viral vector containing modified U11 snRNA
Trade Name
Orphan Indication Duchenne muscular dystrophy
USA Market Approval USA
USA Designation Date 2010-09-15 00:00:00
Sponsor uniQure Biopharma B.V.;Paasheuvelweg 25, 1105 BP;Amsterdam