Exon 52 specific phosphorothiate oligonucleotide | |
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Trade Name | |
Orphan Indication | Duchenne muscular dystrophy |
USA Market Approval | USA |
USA Designation Date | 2013-01-23 00:00:00 |
Sponsor | BioMarin Pharmaceutical, Inc.;105 Digital Drive;Novato, California, 94949 |