recombinant adeno-associated virus serotype AAV8 vector encoding human ornithine transcarbamylase

recombinant adeno-associated virus serotype AAV8 vector encoding human ornithine transcarbamylase
Trade Name
Orphan Indication Ornithine Transcarbamylase Deficiency
USA Market Approval USA
USA Designation Date 2015-12-29 00:00:00
Sponsor Dimension Therapeutics;840 Memorial Drive;Cambridge, Massachusetts, 02139