adeno-associated virus (AAV) serotype rh.10 expressing beta-galactosidase

adeno-associated virus (AAV) serotype rh.10 expressing beta-galactosidase
Trade Name
Orphan Indication Gangliosidosis generalized GM1- type 1
USA Market Approval USA
USA Designation Date 2017-01-30 00:00:00
Sponsor Lysogene, Inc.;245 First Street, 18th Floor;Cambridge, Massachusetts, 02142