recombinant adeno-associated virus vector serotype 9 expressing human N-Sulfoglucosamine Sulfohydrolase

recombinant adeno-associated virus vector serotype 9 expressing human N-Sulfoglucosamine Sulfohydrolase
Trade Name
Orphan Indication Sanfilippo Syndrome
USA Market Approval USA
USA Designation Date 2016-09-01 00:00:00
Sponsor Research Institute at Nationwide Children's Hospital;Center for Gene Therapy, 700 Childrens Drive;Columbus, Ohio, 43205