an adeno-associated viral vector containing a codon-optimised human factor IX gene (AAV5-hFIXco)

an adeno-associated viral vector containing a codon-optimised human factor IX gene (AAV5-hFIXco)
Trade Name
Orphan Indication Hemophilia B
USA Market Approval USA
USA Designation Date 2011-12-22 00:00:00
Sponsor uniQure, B.V.;Meiberdreef 61, 1100 DA;Amsterdam