Exon 55 specific phosphorothioate oligonucleotide

Exon 55 specific phosphorothioate oligonucleotide
Trade Name
Orphan Indication Duchenne muscular dystrophy
USA Market Approval USA
USA Designation Date 2013-01-23 00:00:00
Sponsor BioMarin Pharmaceutical, Inc.;105 Digital Drive;Novato, California, 94949