scAAV9.MeCP2.hCLN3, a self-complementary AAV serotype 9 expressing human CLN3 (hCLN3)

scAAV9.MeCP2.hCLN3, a self-complementary AAV serotype 9 expressing human CLN3 (hCLN3)
Trade Name
Orphan Indication Batten disease
USA Market Approval USA
USA Designation Date 2017-06-27 00:00:00
Sponsor Abeona Therapeutics;6555 Carnegie Blvd, Suite 401;Cleveland, Ohio, 44103