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Treatment Database

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Product Indication Date Designated
Halofantrine Mild to moderate acute malaria caused by susceptible strains of P. falciparum and P. vivax. Nov 04, 1991
Synthetic derivative of 16-hydroxy-9Z, 12Z, 14E-octadecatrienoic acid Prophylactic treatment of sickle cell disease Oct 24, 1991
Lodoxamide tromethamine Vernal keratoconjunctivitis Oct 16, 1991
Dynamine Hereditary motor and sensory neuropathy type I (Charcot-Marie-Tooth disease) Oct 16, 1991
Monoclonal antibody to cytomegalovirus (human) Prophylaxis of cytomegalovirus disease in patients undergoing solid organ transplantation Sep 13, 1991
Filgrastim Patients with AIDS who, in addition, are afflicted with cytomegalovirus retinitis and are being treated with ganciclovir Sep 03, 1991
Mecasermin Amyotrophic lateral sclerosis Aug 05, 1991
mecasermin Amyotrophic lateral sclerosis Aug 05, 1991
Ursodiol Patients with primary biliary cirrhosis Jun 20, 1991
Alpha-galactosidase A Alpha-galactosidase A deficiency (Fabry's disease) Jun 17, 1991
Fosphenytoin For the acute treatment of patients with status epilepticus of the grand mal type Jun 04, 1991
Poly I: poly C12U Renal cell carcinoma May 20, 1991
Interleukin-3 human (recombinant) Promotion of erythropoiesis in Diamond-Blackfan anemia (congenital pure red cell aplasia) May 20, 1991
Recombinant human superoxide dismutase Prevention of bronchopulmonary dysplasia in premature neonates weighing less than 1500 grams Apr 18, 1991
Recombinant secretory leucocyte protease inhibitor Cystic fibrosis Mar 29, 1991
Ursodiol Management of the clinical signs and symptoms associated with primary biliary cirrhosis Feb 19, 1991
Idarubicin HCl for injection Acute lymphoblastic leukemia in pediatric patients Feb 12, 1991
Gentamicin impregnated PMMA beads on surgical wire Chronic osteomyelitis of post-traumatic, postoperative, or hematogenous origin Jan 31, 1991
Pentostatin Patients with chronic lymphocytic leukemia Jan 29, 1991
Cytomegalovirus immune globulin intravenous (human) For use in conjunction with ganciclovir sodium for the treatment of cytomegalovirus pneumonia in bone marrow transplant patients Jan 28, 1991