Treatment Database

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Product Indication Date Designated
Oxaliplatin Ovarian cancer Oct 06, 1992
Secretory leukocyte protease inhibitor Bronchopulmonary dysplasia Jun 30, 1992
Cystic fibrosis gene therapy Cystic fibrosis Jun 30, 1992
Ciliary neurotrophic factor, recombinant human Motor neuron disease (including amyotrophic lateral sclerosis, progressive muscular atrophy, progressive bulbar palsy, and primary lateral sclerosis) May 08, 1992
Sodium Monomercaptoundecahydro-closo-dodecaborate For use in boron neutron capture therapy (BNCT) in the treatment of glioblastoma multiforme Apr 15, 1992
Alitretinoin Acute promyelocytic leukemia Apr 10, 1992
Technetium Tc99m murine monoclonal antibody (IgG2a) to B cell Diagnostic imaging in the evaluation of the extent of disease in patients with histologically confirmed diagnosis of non-Hodgkin's B-cell lymphoma, acute B-cell lymphoblastic leukemia (in children and adults), and chronic B-cell lymphocytic leukemia Apr 07, 1992
Polymeric oxygen Sickle cell anemia Mar 25, 1992
Melphalan For use in hyperthermic regional limb perfusion to treat metastatic melanoma of the extremity Mar 03, 1992
Pilocarpine HCl Xerostomia and keratoconjunctivitis sicca in Sjogren's syndrome patients Feb 28, 1992
Melphalan Patients with multiple myeloma for whom oral therapy is inappropriate Feb 24, 1992
Loxoribine Common variable immunodeficiency Feb 24, 1992
Ciliary neurotrophic factor Amyotrophic lateral sclerosis Jan 30, 1992
Cystic fibrosis transmembrane conductance regulator For cystic fibrosis transmembrane conductance regulator protein replacement therapy in cystic fibrosis patients Jan 14, 1992
Cryptosporidium hyperimmune bovine colostrum IgG concentrate Diarrhea in AIDS patients caused by infection with Cryptosporidium parvum Dec 30, 1991
botulinum toxin type A Dynamic muscle contracture in pediatric cerebral palsy patients Dec 06, 1991
Monoclonal antibody to cytomegalovirus (human) Cytomegalovirus retinitis in patients with AIDS Nov 15, 1991
Halofantrine Mild to moderate acute malaria caused by susceptible strains of P. falciparum and P. vivax. Nov 04, 1991
Synthetic derivative of 16-hydroxy-9Z, 12Z, 14E-octadecatrienoic acid Prophylactic treatment of sickle cell disease Oct 24, 1991
Lodoxamide tromethamine Vernal keratoconjunctivitis Oct 16, 1991