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Treatment Database

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Product Indication Date Designated
Ethinyl Estradiol, USP Turner's syndrome Jun 22, 1988
Coagulation factor VIIa (recombinant) Bleeding episodes in hemophilia A or B patients with inhibitors to Factor VIII or Factor IX Jun 06, 1988
Interferon alfa-2a (recombinant) Renal cell carcinoma Apr 18, 1988
mefloquine HCL For use in the treatment of acute malaria due to Plasmodium falciparum and Plasmodium vivax, and for the prophylaxis of Plasmodium falciparum malaria which is resistant to other available drugs Apr 13, 1988
Levocabastine HCl ophthalmic suspension 0.05% Vernal keratoconjunctivitis Feb 29, 1988
Ceramide trihexosidase/alpha-galactosidase A Fabry's disease Jan 19, 1988
Gamma hydroxybutyrate Narcolepsy and the auxiliary symptoms of cataplexy, sleep paralysis, hypnagogic hallucinations and automatic behavior Dec 03, 1987
Iodine I 131 Lym-1 Monoclonal Antibody B-cell lymphoma Nov 02, 1987
substituted benzaldehyde that binds to the oxy-conformation of Hb between amino terminal residues of the alpha-subunits Sickle cell disease Oct 23, 1987
Pentostatin for injection Hairy cell leukemia Sep 10, 1987
CD5-T lymphocyte immunotoxin Graft versus host disease and/or rejection in patients who have received bone marrow transplants Aug 27, 1987
ST1-RTA immunotoxin (SR 44163) 1. Prevention of acute graft versus host disease in allogenic bone marrow transplantation 2. patients with B-chronic lymphocytic leukemia Aug 12, 1987
Interferon alfa-2b (recombinant) Ovarian carcinoma Aug 03, 1987
Cytomegalovirus immune globulin (human) Prevention or attenuation of primary cytomegalovirus disease in immunosuppressed recipients of organ transplants Aug 03, 1987
Somatropin (rDNA origin) injection 1. growth failure in children due to inadequate growth hormone secretion 2. short stature associated with Turner's syndrome Jul 10, 1987
Interferon alfa-2b (recombinant) Chronic myelogenous leukemia Jun 22, 1987
Somatropin (rDNA origin) Idiopathic or organic growth hormone deficiency in children with growth failure Mar 06, 1987
Calcitonin-human for injection Symptomatic Paget's disease (osteitis deformans) Jan 20, 1987
Teriparatide Diagnostic agent to assist in establishing the diagnosis in patients presenting with clinical and laboratory evidence of hypocalcemia due to either hypoparathyroidism or pseudohypoparathyroidism Jan 09, 1987
Mazindol Duchenne muscular dystrophy Dec 08, 1986