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Treatment Database

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Product Indication Date Designated
Cytomegalovirus immune globulin intravenous (human) For use in conjunction with ganciclovir sodium for the treatment of cytomegalovirus pneumonia in bone marrow transplant patients Jan 28, 1991
Ricin (blocked) conjugated murine mca (anti-b4) For the ex-vivo purging of leukemic cells from the bone marrow of non-T cell acute lymphocytic leukemia patients who are in complete remission Jan 24, 1991
Desmopressin acetate Mild hemophilia A and von Willebrand's disease Jan 22, 1991
Dornase alfa To reduce mucous viscosity and enable the clearance of airway secretions in patients with cystic fibrosis Jan 16, 1991
Mucoid exopolysaccharide Pseudomonas hyperimmune globulin Pulmonary infections due to Pseudomonas aeruginosa in patients with cystic fibrosis Jan 09, 1991
cladribine Chronic lymphocytic leukemia Dec 31, 1990
3,4-diaminopyridine Lambert-Eaton myasthenic syndrome Dec 18, 1990
Amifampridine Lambert-Eaton myasthenic syndrome Dec 18, 1990
amifampridine Lambert-Eaton myasthenic syndrome Dec 18, 1990
Cladribine Hairy cell leukemia Nov 15, 1990
Mucoid exopolysaccharide Pseudomonas hyperimmune globulin Prevention of pulmonary infections due to Pseudomonas aeruginosa in patients with cystic fibrosis Nov 07, 1990
Filgrastim Patients with severe chronic neutropenia (absolute neutrophil count less than 500/mm3) Nov 07, 1990
Succimer Prevention of cystine kidney stone formation in patients with homozygous cystinuria who are prone to stone development Nov 05, 1990
Calcitonin salmon nasal spray Symptomatic Paget's disease (osteitis deformans) Oct 29, 1990
Tretinoin Acute promyelocytic leukemia Oct 24, 1990
Gossypol Cancer of the adrenal cortex Oct 22, 1990
Taxol isolated from Taxus brevifolia Ovarian cancer Oct 15, 1990
Hydroxyurea Patients with sickle cell anemia as shown by the presence of hemoglobin S Oct 01, 1990
Triptorelin pamoate For use in the palliative treatment of advanced ovarian carcinoma of epithelial origin Aug 10, 1990
Liothyronine sodium injection Myxedema coma/precoma Jul 30, 1990