Treatment Database

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Product Indication Date Designated
Trientine HCl Patients with Wilson's disease who are intolerant, or inadequately responsive to penicillamine Dec 24, 1984
Sodium monomercaptoundecahydro-closo-dodecaborate For use in conjunction with a thermal or epithermal neutron beam in boron nuclear capture therapy of glioblastoma multiforme Dec 18, 1984
Antithrombin III (human) For replacement therapy in congenital deficiency of AT-III for prevention and treatment of thrombosis and pulmonary emboli Nov 26, 1984
Spiramycin For symptomatic relief and parasitic cure of chronic cryptosporidiosis in patients with immunodeficiency Oct 17, 1984
Levocarnitine Primary and secondary carnitine deficiency of genetic origin Jul 26, 1984
viloxazine HCL Cataplexy and narcolepsy Jun 11, 1984
Clofazimine Lepromatous leprosy, including dapsone-resistant lepromatous leprosy and lepromatous leprosy complicated by erythema nodosum leprosum Jun 11, 1984
Pegademase bovine For enzyme replacement therapy for ADA deficiency in patients with severe combined immunodeficiency May 29, 1984
Ethanolamine oleate Patients with esophageal varices that have recently bled, to prevent rebleeding Mar 22, 1984
Hemin Amelioration of recurrent attacks of acute intermittent porphyria (AIP) temporarily related to the menstrual cycle in susceptible women and similar symptoms which occur in other patients with AIP, porphyria variegata and hereditary coproporphyria Mar 16, 1984