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Treatment Database

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Product Indication Date Designated
N-(4-Fluoro-benzoyl)-L-arginyl-L-arginyl-[L-3-(naphthyl)alanyl]-L-cysteinyl-L-tyrosyl-L-citrullinyl-L-lysyl-D-lysyl-L-prolyl-L-trosyl-L-arginyl-L-ctrullinyl-L-cysteinyl-L-aginine amide,cyclic (4-13)-disulfide Pancreatic cancer Feb 01, 2019
Fully human immunoglobulin G1 monoclonal antibody that targets CD32b Mantle cell lymphoma Jan 29, 2019
delta-9-tetrahydrocannabinol and cannabidiol Huntington's Disease Jan 29, 2019
Losartan Epidermolysis bullosa Jan 29, 2019
internalized-arginylglycylaspartic acid cyclic peptide Pancreatic cancer Jan 29, 2019
5,7-Dichloro-2-((ethylamino)methyl)-8-hydroxy-3-methylquinazolin-4(3H)-one mesylate Multiple system atrophy Jan 29, 2019
clofarabine Acute myeloid leukemia Jan 24, 2019
[2-amino-3-[3-[[4-(2-pyridyloxymethyl)phenyl]methyl]isoxazol-5-yl]pyridin-1-ium-1-yl]methyl hydrogen phosphate Cryptococcosis Jan 22, 2019
Human IgG1 monoclonal antibody to human CD38 Multiple myeloma Jan 22, 2019
recombinant Mitsugumin 53 Duchenne Muscular Dystrophy Jan 17, 2019
tiratricol Monocarboxylate 8 Transporter (MCT8) Deficiency (Allan-Herndon-Dudley-Syndrome) Jan 16, 2019
adeno-associated viral vector 9-containing the human heparan-alpha-glucosaminide N-acetyltransferase (HGSNAT) gene (AAV9- HGSNAT) Sanfilippo Syndrome IIIC (also known as Mucopolysaccharidosis IIIC/MPS IIIC) Jan 16, 2019
ribitol Limb-girdle muscular dystrophy type 2I Jan 16, 2019
odevixibat Biliary Atresia Jan 16, 2019
N-(bromoacetyl)-3,3-dinitroazetidine Glioblastoma multiforme Jan 16, 2019
D-Galactose Phosphoglucomutase 1 Deficiency Jan 14, 2019
cusatuzumab Acute myeloid leukemia Jan 14, 2019
Autotaxin inhibitor Idiopathic Pulmonary Fibrosis Jan 14, 2019
2-(5-(2-((2,3-dihydro-1H-inden-2-yl)amino)pyrimidin-5-yl)-1,3,4-oxadiazol-2-yl)-1-(1,4,6,7-tetrahydro-5H-[1,2,3]triazolo[4,5-c]pyridin-5-yl)ethan-1-one Idiopathic Pulmonary Fibrosis Jan 14, 2019
Ralinepag Pulmonary arterial hypertension Jan 11, 2019