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Treatment Database

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Product Indication Date Designated
adoptive, anti-FLT3 chimeric antigen receptor T cell therapy generated through transduction of autologous T-cells with a self-inactivating human immunodeficiency virus-1 based lentiviral vector Acute myeloid leukemia Jun 13, 2019
cytarabine-beta-L-aspartic acid Acute Myeloid Leukemia May 14, 2019
N-{2-[N-((3S)(3-piperidyl))carbamoyl]-5-[2-(3-fluorophenyl)ethynyl](3-thienyl)}aminoamide Acute myeloid leukemia Apr 29, 2019
A small molecule inhibitor of the pro-survival protein Myeloid Cell Leukemia sequence 1 (MCL 1) Acute Myeloid Leukemia Feb 15, 2019
clofarabine Acute myeloid leukemia Jan 24, 2019
cusatuzumab Acute myeloid leukemia Jan 14, 2019
ceramide Acute Myeloid Leukemia Dec 18, 2018
venetoclax + idasanutlin Acute myeloid leukemia Dec 17, 2018
8-bromo-2-(1-methylpiperidin-4-yl) amino)-4-(4-phenoxyphenyl) amino) pyrido[4,3-d] pyrimidin-5(6H)-one hydrochloride Acute Myeloid Leukemia Nov 20, 2018
5-Chloro-N-(3-cyclopropyl-5-(((3R,5S)-3,5-dimethylpiperazine-1-yl)methyl)phenyl)-4-(6-methyl-1H-indol-3-yl)pyrimidin-2-amine�monohydrate Acute Myeloid Leukemia Oct 25, 2018
Indolino-benzodiazepine compound (sulfonated DGN549-C) conjugated to the humanized anti-CD123 monoclonal antibody (G4723A) Acute myeloid leukemia Oct 10, 2018
2-(3,5-difluoro-3'-methoxybiphenyl-4-ylamino)nicotinic acid Acute myeloid leukemia Aug 16, 2018
apomorphine palmitate Acute Myeloid Leukemia Jun 04, 2018
Indolino-benzodiazepine compound (sulfonated DGN462) conjugated to the humanized anti-CD33 monoclonal antibody (Z4681A) via the sulfo-SPDB linker Acute myeloid leukemia May 02, 2018
Cell-penetrating activating transcription factor 5 mimetic Acute Myeloid Leukemia Apr 30, 2018
7-(4-fluoro-2-methoxyphenyl)-6-methyl-N-(1-(piperidin-4-yl)-1H-pyrazol-4-yl) thieno [3,2-d]pyrimidin-2-amine semi-fumarate Acute myeloid leukemia Mar 26, 2018
1-{3-fluoro-4-[7-(5-methyl-lH-imidazol-2-yl)- 1-oxo-2,3-dihydro-lH-isoindo 1-4-yl]-phenyl}-3-(3-trifluoromethyl-phenyl)-urea Acute myeloid leukemia (AML) Dec 22, 2017
Urea, N-[4-[2,3-dihydro-7-(5-methyl-1H-imidazol-2-yl)-1-oxo-1H-isoindol-4-yl]-3-fluorophenyl]-N�-(2,4,6-trifluorophenyl)- Acute myeloid leukemia (AML) Dec 22, 2017
2-O, 3-O, desulfated heparin Acute myeloid leukemia Dec 21, 2017
THIOMAB antibody drug conjugate comprised of humanized IgG1 anti-C-type lectin-like molecule-1 monoclonal antibody and DNA alkylating cross-linking agent pyrrolo [2,1-c][1,4] benzodiazepine dimer Acute myeloid leukemia Oct 24, 2017