Gene-therapy for GAN at NIH

14-year old Gillian was the second person in the world to get an incredible gift: leading-edge gene-therapy treatment for giant axonal neuropathy (or GAN) at the National Institutes of Health (NIH) Clinical Center

According to his mom, that single moment when he received “the golden injection,” transformed everything for her son and his family. “Now, Gillian gets to have a life,” she said.