Close
Close
The Orphan Drug Act: What Does "Orphan" Mean?
337 views
2.85714285714
2.9 from 7 votes

Douglas Paul, PharmD, PhD discusses the Orphan Drug Act and what the term “Orphan” means in context of the the Rare Disease industry, especially considering that much of the Rare Disease pipeline is for Oncology products.

The Orphan Drug Act was first enacted in the United States in 1983 and was set up to encourage the development of drugs for rare diseases. At that time, drug therapies for these disorders were rarely developed. Thirty four years later, a growing proportion of industry research and development and drug approvals target diseases affecting fewer than 200,000 persons in the United States, the prevalence-based threshold of rare disease under the Act.

Most of the policy response to the orphan drug pricing problem has been to explore new ways to evaluate orphan drug performance following regulatory approval. However, there is little indication that health care payers are successfully pushing back on drug price points.

by Abidemi Uruejoma
11 views 5 days ago
by Abidemi Uruejoma
17 views 2 weeks ago
by Abidemi Uruejoma
37 views 3 weeks ago
by Abidemi Uruejoma
47 views 4 weeks ago
by Abidemi Uruejoma
47 views 1 month ago
by Abidemi Uruejoma
51 views 1 month ago
by Abidemi Uruejoma
54 views 1 month ago
by Abidemi Uruejoma
67 views 1 month ago
by Abidemi Uruejoma
66 views 1 month ago
2.85714285714
2.9 from 7 votes
Free Newsletter
Find a Clinical Trial
Related Videos
by Abidemi Uruejoma
286 views
News Articles