By Raffaele Pereno – PhD, MBA BASEL, Switzerland – At BioTechX Europe 2026, CheckOrphan met Dr. Mamadou Bamba, a researcher at De Montfort University in Leicester, UK, whose work explores how artificial intelligence (AI) could help identify biomarkers for rare diseases. His research into Niemann–Pick disease type C1 (NPC1) highlights...

COPENHAGEN, Denmark — Ascendis Pharma A/S (Nasdaq: ASND) today announced that the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has adopted a positive opinion recommending marketing authorization for once-weekly TransCon CNP (navepegritide) in the European Union for the treatment of achondroplasia in children...

MELBOURNE, Australia — Propanc Biopharma, Inc. (Nasdaq: PPCB) (“Propanc” or the “Company”), a biopharmaceutical company focused on developing novel treatments for chronic diseases including recurrent and metastatic cancer, today announced new preclinical research from an academic–industry collaboration from the Universities of Jaén and Granada, led by Dr. Maria Belén Toledo,...